Efficient gene editing of human long-term hematopoietic stem cells validated by clonal tracking-Reference-Cited by-同舟云学术

Efficient gene editing of human long-term hematopoietic stem cells validated by clonal tracking

Published:2020-06-29 Issue:11 Volume:38 Page:1298-1308
ISSN:1087-0156
Container-title:Nature Biotechnology
language:en
Short-container-title:Nat Biotechnol

Author:

Ferrari Samuele^ORCID,Jacob Aurelien^ORCID,Beretta Stefano^ORCID,Unali Giulia,Albano Luisa,Vavassori Valentina^ORCID,Cittaro Davide^ORCID,Lazarevic Dejan,Brombin Chiara,Cugnata Federica,Kajaste-Rudnitski Anna^ORCID,Merelli Ivan,Genovese Pietro^ORCID,Naldini Luigi^ORCID

Publisher

Springer Science and Business Media LLC

Subject

Biomedical Engineering,Molecular Medicine,Applied Microbiology and Biotechnology,Bioengineering,Biotechnology

Link

http://www.nature.com/articles/s41587-020-0551-y.pdf

Reference60 articles.

1. Naldini, L. Genetic engineering of hematopoiesis: current stage of clinical translation and future perspectives. EMBO Mol. Med. https://doi.org/10.15252/emmm.201809958 (2019).

2. Carroll, D. Genome engineering with targetable nucleases. Annu. Rev. Biochem. 83, 409–439 (2014).

3. Genovese, P. et al. Targeted genome editing in human repopulating haematopoietic stem cells. Nature 510, 235–240 (2014).

4. Schiroli, G. et al. Preclinical modeling highlights the therapeutic potential of hematopoietic stem cell gene editing for correction of SCID-X1. Sci. Transl. Med. 9, (2017).

5. Boitano, A. E. et al. Aryl hydrocarbon receptor antagonists promote the expansion of human hematopoietic stem cells. Science 329, 1345–1348 (2010).

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