Targeted genome editing in human repopulating haematopoietic stem cells-Reference-Cited by-同舟云学术

Targeted genome editing in human repopulating haematopoietic stem cells

Published:2014-05-28 Issue:7504 Volume:510 Page:235-240
ISSN:0028-0836
Container-title:Nature
language:en
Short-container-title:Nature

Author:

Genovese Pietro,Schiroli Giulia,Escobar Giulia,Di Tomaso Tiziano,Firrito Claudia,Calabria Andrea,Moi Davide,Mazzieri Roberta,Bonini Chiara,Holmes Michael C.,Gregory Philip D.,van der Burg Mirjam,Gentner Bernhard,Montini Eugenio,Lombardo Angelo,Naldini Luigi

Publisher

Springer Science and Business Media LLC

Subject

Multidisciplinary

Link

http://www.nature.com/articles/nature13420.pdf

Reference43 articles.

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3. Cavazzana-Calvo, M. et al. Transfusion independence and HMGA2 activation after gene therapy of human β-thalassaemia. Nature 467, 318–322 (2010)

4. Cartier, N. et al. Hematopoietic stem cell gene therapy with a lentiviral vector in X-linked adrenoleukodystrophy. Science 326, 818–823 (2009)

5. Biffi, A. et al. Lentiviral hematopoietic stem cell gene therapy benefits metachromatic leukodystrophy. Science 341, 1233158 (2013)

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