Sleeping Beauty mRNA-LNP enables stable rAAV transgene expression in mouse and NHP hepatocytes and improves vector potency-Reference-Cited by-同舟云学术

Sleeping Beauty mRNA-LNP enables stable rAAV transgene expression in mouse and NHP hepatocytes and improves vector potency

Published:2024-07 Issue: Volume: Page:
ISSN:1525-0016
Container-title:Molecular Therapy
language:en
Short-container-title:Molecular Therapy

Author:

Zakas Philip M.,Cunningham Sharon C.,Doherty Ann,van Dijk Eva B.,Ibraheim Raed,Yu Stephanie,Mekonnen Befikadu D.,Lang Brendan,English Elizabeth J.,Sun Gang,Duncan Miles C.,Benczkowski Matthew S.,Altshuler Robert C.,Singh Malvenderjit Jagjit,Kibbler Emily S.,Tonga Gulen Y.,Wang Zi Jun,Wang Z. Jane,Li Guangde,An Ding,Rottman James B.,Bhavsar Yashvi,Purcell Cormac,Jain Rachit,Alberry Ryan,Roquet Nathaniel,Fu Yanfang,Citorik Robert J.,Rubens Jacob R.,Holmes Michael C.,Cotta-Ramusino Cecilia,Querbes William,Alexander Ian E.,Salomon William E.^ORCID

Publisher

Elsevier BV

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