Focused Update on AAV-Based Gene Therapy Clinical Trials for Inherited Retinal Degeneration
Author:
Publisher
Springer Science and Business Media LLC
Subject
Pharmacology (medical),Pharmacology,General Medicine,Biotechnology
Link
http://link.springer.com/content/pdf/10.1007/s40259-020-00453-8.pdf
Reference184 articles.
1. Diaz-Coranguez M, Ramos C, Antonetti DA. The inner blood-retinal barrier: cellular basis and development. Vis Res. 2017;139:123–37.
2. Bennett J. Immune response following intraocular delivery of recombinant viral vectors. Gene Ther. 2003;10(11):977–82.
3. Hellstrom M, Harvey AR. Retinal ganglion cell gene therapy and visual system repair. Curr Gene Ther. 2011;11(2):116–31.
4. Ochakovski GA, Bartz-Schmidt KU, Fischer MD. Retinal gene therapy: surgical vector delivery in the translation to clinical trials. Front Neurosci. 2017;11:174.
5. Jolly JK, Bridge H, MacLaren RE. Outcome measures used in ocular gene therapy trials: a scoping review of current practice. Front Pharmacol. 2019;10:1076.
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