1. San Raffaele Telethon Institute for Gene Therapy (TIGET), San Raffaele Scientific Institute, 20132 Milan, Italy.
2. TIGET Pediatric Clinical Research Unit, Division of Regenerative Medicine, Stem Cells and Gene Therapy, San Raffaele Scientific Institute, 20132 Milan, Italy.
3. Pediatric Immunohematology and Bone Marrow Transplant Unit, San Raffaele Scientific Institute, 20132 Milan, Italy.
4. Vita-Salute San Raffaele University, 20132 Milan, Italy.
5. Neurology Unit, Department of Neurology, San Raffaele Scientific Institute, 20132 Milan, Italy.
6. Neuroradiology Unit, Head and Neck Department, San Raffaele Scientific Institute, 20132 Milan, Italy.
7. Department of Experimental Medicine and Biochemical Sciences, University of Perugia, 06122 Perugia, Italy.
8. MolMed, 20132 Milan, Italy.
9. Distributed Computing Group, Center for Advanced Studies, Research and Development in Sardinia (CRS4), 09010 Pula, Italy.
10. Pediatric Hematology Oncology Division, Rafic Hariri University Hospital, Beirut, Lebanon.
11. Department of Pediatrics, University of Nebraska Medical Center, Omaha, NE 68198, USA.
12. Molecular and Cellular Technologies, GlaxoSmithKline, Stevenage 5G1 2NY, UK.
13. Pediatric Blood and Marrow Transplantation Program, University Medical Center 3584 CX Utrecht, Netherlands.
14. Department of Translational Oncology, National Center for Tumor Diseases and German Cancer Research Center, 69120 Heidelberg, Germany.
15. Hematology and Bone Marrow Transplant Unit, San Raffaele Scientific Institute, 20132 Milan, Italy.
16. Center for Translational Genomics and BioInformatics, San Raffaele Scientific Institute, 20132 Milan, Italy.
17. Regenerative Medicine Discovery Performance Unit, GlaxoSmithKline Research and Development, King of Prussia, PA 19406, USA.
18. Bone Marrow Transplant Unit, MBBM Foundation, Pediatric Department, Milano-Bicocca University at San Gerardo Hospital, 20052 Monza, Italy.
19. University of Rome Tor Vergata, 00133 Rome, Italy.