Targeted knock-in of NCF1 cDNA into the NCF2 locus leads to myeloid phenotypic correction of p47 -deficient chronic granulomatous disease
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Published:2024-09
Issue:3
Volume:35
Page:102229
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ISSN:2162-2531
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Container-title:Molecular Therapy - Nucleic Acids
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language:en
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Short-container-title:Molecular Therapy - Nucleic Acids
Author:
Siow Kah MunORCID,
Güngör Merve,
Wrona Dominik,
Raimondi Federica,
Pastukhov Oleksandr,
Tsapogas Panagiotis,
Menzi Timon,
Schmitz Michael,
Kulcsár Péter István,
Schwank Gerald,
Schulz Ansgar,
Jinek Martin,
Modlich Ute,
Siler Ulrich,
Reichenbach JanineORCID