An update on RNA-targeting therapies for neuromuscular disorders
Author:
Publisher
Ovid Technologies (Wolters Kluwer Health)
Subject
Clinical Neurology,Neurology
Reference46 articles.
1. Pharmacology of a central nervous system delivered 2-O-methoxyethyl-modified survival of motor neuron splicing oligonucleotide in mice and nonhuman primates.;Rigo;J Pharmacol Exp Ther,2014
2. Theoretic applicability of antisense-mediated exon skipping for Duchenne muscular dystrophy mutations.;Aartsma-Rus;Hum Mutat,2009
3. The TREAT-NMD DMD Global Database: analysis of more than 7,000 Duchenne muscular dystrophy mutations.;Bladen;Hum Mutat,2015
4. Exon skipping and dystrophin restoration in patients with Duchenne muscular dystrophy after systemic phosphorodiamidate morpholino oligomer treatment: an open-label, phase 2, dose-escalation study.;Cirak;Lancet,2011
5. Eteplirsen for the treatment of Duchenne muscular dystrophy.;Mendell;Ann Neurol,2013
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