Eteplirsen for the treatment of Duchenne muscular dystrophy

Author:

Mendell Jerry R.1234,Rodino‐Klapac Louise R.14,Sahenk Zarife1234,Roush Kandice5,Bird Loren5,Lowes Linda P.4,Alfano Lindsay4,Gomez Ann Maria14,Lewis Sarah14,Kota Janaiah14,Malik Vinod14,Shontz Kim14,Walker Christopher M.146,Flanigan Kevin M.1234,Corridore Marco7,Kean John R.47,Allen Hugh D.14,Shilling Chris134,Melia Kathleen R.8,Sazani Peter8,Saoud Jay B.8,Kaye Edward M.8,

Affiliation:

1. Departments of PediatricsOhio State UniversityColumbus OH

2. Neurology the Ohio State UniversityOhio State UniversityColumbus OH

3. Gene Therapy CenterNationwide Children's Hospital Ohio State UniversityColumbus OH

4. Paul D. Wellstone CenterNationwide Children's Hospital Ohio State UniversityColumbus OH

5. Department of Pediatrics Clinical Research ServicesNationwide Children's Hospital Ohio State UniversityColumbus OH

6. Center for Vaccines and ImmunityNationwide Children's Hospital Ohio State UniversityColumbus OH

7. Departments of Surgery and AnesthesiologyNationwide Children's HospitalColumbus OH

8. Sarepta TherapeuticsCambridge MA

Publisher

Wiley

Subject

Neurology (clinical),Neurology

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