Practical Considerations for Delandistrogene Moxeparvovec Gene Therapy in Patients With Duchenne Muscular Dystrophy
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Published:2024-04
Issue:
Volume:153
Page:11-18
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ISSN:0887-8994
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Container-title:Pediatric Neurology
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language:en
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Short-container-title:Pediatric Neurology
Author:
Mendell Jerry R.,
Proud Crystal,
Zaidman Craig M.,
Mason StefanieORCID,
Darton Eddie,
Wang Shufang,
Wandel Christoph,
Murphy Alexander P.ORCID,
Mercuri Eugenio,
Muntoni Francesco,
McDonald Craig M.
Funder
F. Hoffmann-La Roche
Sarepta Therapeutics
F Hoffmann-La Roche Ltd
Cited by
5 articles.
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