Pharmacology of a Central Nervous System Delivered 2′-O-Methoxyethyl–Modified Survival of Motor Neuron Splicing Oligonucleotide in Mice and Nonhuman Primates

Author:

Rigo Frank,Chun Seung J.,Norris Daniel A.,Hung Gene,Lee Sam,Matson John,Fey Robert A.,Gaus Hans,Hua Yimin,Grundy John S.,Krainer Adrian R.,Henry Scott P.,Bennett C. Frank

Publisher

American Society for Pharmacology & Experimental Therapeutics (ASPET)

Subject

Pharmacology,Molecular Medicine

Reference54 articles.

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