Hyperactivity of factor IX Padua (R338L) depends on factor VIIIa cofactor activity
Author:
Funder
NHLBI
Pfizer
HTRS
Bayer
Publisher
American Society for Clinical Investigation
Subject
General Medicine
Link
https://insight.jci.org/articles/view/128683/files/pdf
Reference50 articles.
1. Successful transduction of liver in hemophilia by AAV-Factor IX and limitations imposed by the host immune response
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3. Long-Term Safety and Efficacy of Factor IX Gene Therapy in Hemophilia B
4. Adenovirus-Associated Virus Vector–Mediated Gene Transfer in Hemophilia B
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