Deciphering conundrums of adeno-associated virus liver-directed gene therapy: focus on hemophilia
Author:
Funder
Bayer Fund
Bayer
BioMarin Pharmaceutical
Publisher
Elsevier BV
Subject
Hematology
Reference220 articles.
1. Adeno-associated virus vector as a platform for gene therapy delivery;Wang;Nat Rev Drug Discov,2019
2. Gene therapy advances: a meta-analysis of AAV usage in clinical settings;Au;Front Med (Lausanne),2021
3. The AIDS epidemic in haemophilia patients II: pursuing absolute viral safety of clotting factor concentrates 1985-1988;Evatt;Haemophilia,2012
4. Expression of active human factor VIII from recombinant DNA clones;Wood;Nature,1984
5. Structure of human factor VIII;Vehar;Nature,1984
Cited by 2 articles. 订阅此论文施引文献 订阅此论文施引文献,注册后可以免费订阅5篇论文的施引文献,订阅后可以查看论文全部施引文献
1. Drug‐induced liver injury related to gene therapy: A new challenge to be managed;Liver International;2024-09-09
2. Current and emerging gene therapies for haemophilia A and B;Haemophilia;2024-03-25
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