Circumventing furin enhances factor VIII biological activity and ameliorates bleeding phenotypes in hemophilia models-Reference-Cited by-同舟云学术

Circumventing furin enhances factor VIII biological activity and ameliorates bleeding phenotypes in hemophilia models

Published:2016-10-06 Issue:16 Volume:1 Page:
ISSN:2379-3708
Container-title:JCI Insight
language:en
Short-container-title:

Author:

Siner Joshua I.,Samelson-Jones Benjamin J.,Crudele Julie M.,French Robert A.,Lee Benjamin J.,Zhou Shanzhen,Merricks Elizabeth,Raymer Robin,Nichols Timothy C.,Camire Rodney M.,Arruda Valder R.

Publisher

American Society for Clinical Investigation

Subject

General Medicine

Reference73 articles.

1. Long-Term Safety and Efficacy of Factor IX Gene Therapy in Hemophilia B

2. Adenovirus-Associated Virus Vector–Mediated Gene Transfer in Hemophilia B

3. Obstacles and future of gene therapy for hemophilia

4. Multiyear therapeutic benefit of AAV serotypes 2, 6, and 8 delivering factor VIII to hemophilia A mice and dogs

5. Efficacy and Safety of Long-term Prophylaxis in Severe Hemophilia A Dogs Following Liver Gene Therapy Using AAV Vectors

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