AAV gene therapy in companion dogs with severe hemophilia: Real-world long-term data on immunogenicity, efficacy, and quality of life-Reference-Cited by-同舟云学术

AAV gene therapy in companion dogs with severe hemophilia: Real-world long-term data on immunogenicity, efficacy, and quality of life

Published:2024-03 Issue:1 Volume:32 Page:101205
ISSN:2329-0501
Container-title:Molecular Therapy - Methods & Clinical Development
language:en
Short-container-title:Molecular Therapy - Methods & Clinical Development

Author:

Doshi Bhavya S.^ORCID,Samelson-Jones Benjamin J.,Nichols Timothy C.,Merricks Elizabeth P.,Siner Joshua I.,French Robert A.,Lee Ben J.,Arruda Valder R.,Callan Mary Beth

Funder

National Center for Advancing Translational Sciences

Institute for Translational Medicine and Therapeutics

National Heart Lung and Blood Institute Division of Intramural Research

Publisher

Elsevier BV

Reference46 articles.

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3. Animal models of hemophilia;Sabatino;Prog. Mol. Biol. Transl. Sci.,2012

4. Protein replacement therapy and gene transfer in canine models of hemophilia A, hemophilia B, von willebrand disease, and factor VII deficiency;Nichols;ILAR J./National Research Council, Institute of Laboratory Animal Resources,2009

5. Canine models of inherited bleeding disorders in the development of coagulation assays, novel protein replacement and gene therapies;Nichols;J. Thromb. Haemost.,2016

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