Safety evaluation of 2′-deoxy-2′-fluoro nucleotides in GalNAc-siRNA conjugates
Author:
Affiliation:
1. Alnylam Pharmaceuticals, Inc., Cambridge, MA 02142, USA
Funder
Alnylam Pharmaceuticals
Publisher
Oxford University Press (OUP)
Subject
Genetics
Link
http://academic.oup.com/nar/article-pdf/47/7/3306/28467977/gkz140.pdf
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4. Targeting of antithrombin in hemophilia A or B with RNAi therapy;Pasi;N. Engl. J. Med.,2017
5. Clinical proof of concept for a novel Hepatocyte-Targeting GalNAc-siRNA conjugate;Zimmermann;Mol. Ther.,2017
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