Patisiran, an RNAi Therapeutic, for Hereditary Transthyretin Amyloidosis

Author:

Adams David1,Gonzalez-Duarte Alejandra1,O’Riordan William D.1,Yang Chih-Chao1,Ueda Mitsuharu1,Kristen Arnt V.1,Tournev Ivailo1,Schmidt Hartmut H.1,Coelho Teresa1,Berk John L.1,Lin Kon-Ping1,Vita Giuseppe1,Attarian Shahram1,Planté-Bordeneuve Violaine1,Mezei Michelle M.1,Campistol Josep M.1,Buades Juan1,Brannagan Thomas H.1,Kim Byoung J.1,Oh Jeeyoung1,Parman Yesim1,Sekijima Yoshiki1,Hawkins Philip N.1,Solomon Scott D.1,Polydefkis Michael1,Dyck Peter J.1,Gandhi Pritesh J.1,Goyal Sunita1,Chen Jihong1,Strahs Andrew L.1,Nochur Saraswathy V.1,Sweetser Marianne T.1,Garg Pushkal P.1,Vaishnaw Akshay K.1,Gollob Jared A.1,Suhr Ole B.1

Affiliation:

1. From Assistance Publique–Hôpitaux de Paris (APHP), National Reference Center for Familial Amyloidotic Polyneuropathy, Centre Hospitalier Universitaire (CHU) Bicêtre, INSERM Unité 1195, Université Paris-Sud, Le Kremlin-Bicêtre (D.A.), the Department of Neuromuscular Disorders and ALS, Hôpital de la Timone, Marseille (S.A.), and the Department of Neurology, Amyloid Network, CHU Henri Mondor–APHP, Créteil (V.P.-B.) — all in France; the National Institute of Medical Sciences and Nutrition–Salvador Zubiran,...

Funder

Alnylam Pharmaceuticals

Publisher

Massachusetts Medical Society

Subject

General Medicine

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