Stem Cell Therapy for the Central Nervous System in Lysosomal Storage Diseases-Reference-Cited by-同舟云学术

Stem Cell Therapy for the Central Nervous System in Lysosomal Storage Diseases

Published:2016-10 Issue:10 Volume:27 Page:749-757
ISSN:1043-0342
Container-title:Human Gene Therapy
language:en
Short-container-title:Human Gene Therapy

Author:

Siddiqi Faez¹,Wolfe John H.¹²

Affiliation:

1. Research Institute of Children's Hospital of Philadelphia, Philadelphia, Pennsylvania

2. Department of Pediatrics, Perelman School of Medicine and W.F. Goodman Center for Comparative Medical Genetics, School of Veterinary Medicine, University of Pennsylvania, Philadelphia, Pennsylvania.

Publisher

Mary Ann Liebert Inc

Subject

Genetics,Molecular Biology,Molecular Medicine

Link

http://www.liebertpub.com/doi/pdf/10.1089/hum.2016.088

Reference120 articles.

1. Treatment of lysosomal storage disorders: successes and challenges

2. Inherited neurodegenerative diseases: the one-hit model of neurodegeneration

3. Lysosomal storage diseases: Diagnostic confirmation and management of presymptomatic individuals

4. Neural stem cells - a versatile tool for cell replacement and gene therapy in the central nervous system

5. Neural Stem Cell Transplantation as a Therapeutic Approach for Treating Lysosomal Storage Diseases

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1. Targeting the central nervous system in lysosomal storage diseases: Strategies to deliver therapeutics across the blood-brain barrier;Molecular Therapy;2023-03

2. The Challenge of Gene Therapy for Neurological Diseases: Strategies and Tools to Achieve Efficient Delivery to the Central Nervous System;Human Gene Therapy;2021-04-01

3. Humoral Influence of Repeated Lineage-Negative Stem/Progenitor Cell Administration on Articulatory Functions in ALS Patients;Stem Cells International;2020-12-14

4. Improvement of motor and behavioral activity in Sandhoff mice transplanted with human CD34+ cells transduced with a HexA/HexB expressing lentiviral vector;The Journal of Gene Medicine;2020-05-07

5. Runx1t1 promotes the neuronal differentiation in rat hippocampus;Stem Cell Research & Therapy;2020-04-22