The Challenge of Gene Therapy for Neurological Diseases: Strategies and Tools to Achieve Efficient Delivery to the Central Nervous System-Reference-Cited by-同舟云学术

The Challenge of Gene Therapy for Neurological Diseases: Strategies and Tools to Achieve Efficient Delivery to the Central Nervous System

Published:2021-04-01 Issue:7-8 Volume:32 Page:349-374
ISSN:1043-0342
Container-title:Human Gene Therapy
language:en
Short-container-title:Human Gene Therapy

Author:

Piguet Françoise¹,de Saint Denis Timothée¹²,Audouard Emilie¹,Beccaria Kevin¹²,André Arthur¹³,Wurtz Guillaume¹,Schatz Raphael¹,Alves Sandro⁴,Sevin Caroline¹⁴⁵,Zerah Michel¹²,Cartier Nathalie¹

Affiliation:

1. NeuroGenCell, INSERM U1127, Paris Brain Institute (ICM), Sorbonne University, CNRS, AP-HP, University Hospital Pitié-Salpêtrière, Paris, France

2. APHP, Department of Pediatric Neurosurgery, Hôpital Necker-Enfants Malades, APHP Centre. Université de Paris, Paris, France

3. APHP, Department of Neurosurgery, Hôpitaux Universitaires La Pitié-Salpêtrière, Sorbonne Universités, UPMC Univ Paris 6, Paris, France

4. BrainVectis—Askbio France, iPeps Paris Brain Institute, Paris, France

5. APHP, Department of Neurology, Hopital le Kremlin Bicetre, Paris, France.

Publisher

Mary Ann Liebert Inc

Subject

Genetics,Molecular Biology,Molecular Medicine

Link

https://www.liebertpub.com/doi/pdf/10.1089/hum.2020.105

Reference208 articles.

1. The Blood–Brain Barrier

2. The Blood-Brain Barrier in Health and Chronic Neurodegenerative Disorders

3. Adeno-Associated Virus-Based Gene Therapy for CNS Diseases

4. Genomics in neurodevelopmental disorders: an avenue to personalized medicine

5. Gene therapy and neurodevelopmental disorders

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