In vivo and ex vivo gene therapy for neurodegenerative diseases: a promise for disease modification
Author:
Funder
Shiraz University of Medical Sciences
Publisher
Springer Science and Business Media LLC
Link
https://link.springer.com/content/pdf/10.1007/s00210-024-03141-4.pdf
Reference267 articles.
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2. Abdelnour SA et al (2021) The potential of CRISPR/Cas9 gene editing as a treatment strategy for inherited diseases. Front Cell Dev Biol 9:699597
3. Acsadi G et al (2002) Increased survival and function of SOD1 mice after glial cell-derived neurotrophic factor gene therapy. Hum Gene Ther 13(9):1047–1059
4. Alarcón-Arís D et al (2018) Selective α-synuclein knockdown in monoamine neurons by intranasal oligonucleotide delivery: potential therapy for Parkinson’s disease. Mol Ther 26(2):550–567
5. Alarcón-Arís D et al (2020) Anti-α-synuclein ASO delivered to monoamine neurons prevents α-synuclein accumulation in a Parkinson’s disease-like mouse model and in monkeys. EBioMedicine 59:102944
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