Targeting the central nervous system in lysosomal storage diseases: Strategies to deliver therapeutics across the blood-brain barrier
Author:
Publisher
Elsevier BV
Subject
Drug Discovery,Pharmacology,Genetics,Molecular Biology,Molecular Medicine
Reference197 articles.
1. Lysosomal storage diseases;Platt;Nat. Rev. Dis. Primers,2018
2. The birth prevalence of lysosomal storage disorders in the Czech Republic: comparison with data in different populations;Poupetová;J. Inherit. Metab. Dis.,2010
3. New biotechnological and nanomedicine strategies for treatment of lysosomal storage disorders;Muro;Wiley Interdiscip. Rev. Nanomed Nanobiotechnol,2010
4. Gene therapy for lysosomal storage disorders;Gritti;Expert Opin. Biol. Ther.,2011
5. Lysosomal enzyme replacement therapies: historical development, clinical outcomes, and future perspectives;Solomon;Adv. Drug Deliv. Rev.,2017
Cited by 6 articles. 订阅此论文施引文献 订阅此论文施引文献,注册后可以免费订阅5篇论文的施引文献,订阅后可以查看论文全部施引文献
1. Developing a scoring system for gene curation prioritization in lysosomal diseases;Molecular Genetics and Metabolism;2024-09
2. Targeting Neurological Aspects of Mucopolysaccharidosis Type II: Enzyme Replacement Therapy and Beyond;BioDrugs;2024-08-23
3. Predicting blood–brain barrier permeability of molecules with a large language model and machine learning;Scientific Reports;2024-07-09
4. Challenges and opportunities in neurometabolic disease treatment with enzyme delivery;Expert Opinion on Drug Delivery;2024-06-02
5. First-in-human single-dose study of nizubaglustat, a dual inhibitor of ceramide glucosyltransferase and non-lysosomal glucosylceramidase: Safety, tolerability, pharmacokinetics, and pharmacodynamics of single ascending and multiple doses in healthy adults;Molecular Genetics and Metabolism;2024-01
1.学者识别学者识别
2.学术分析学术分析
3.人才评估人才评估
"同舟云学术"是以全球学者为主线,采集、加工和组织学术论文而形成的新型学术文献查询和分析系统,可以对全球学者进行文献检索和人才价值评估。用户可以通过关注某些学科领域的顶尖人物而持续追踪该领域的学科进展和研究前沿。经过近期的数据扩容,当前同舟云学术共收录了国内外主流学术期刊6万余种,收集的期刊论文及会议论文总量共计约1.5亿篇,并以每天添加12000余篇中外论文的速度递增。我们也可以为用户提供个性化、定制化的学者数据。欢迎来电咨询!咨询电话:010-8811{复制后删除}0370
www.globalauthorid.com
TOP
Copyright © 2019-2024 北京同舟云网络信息技术有限公司 京公网安备11010802033243号 京ICP备18003416号-3