1. Blood-Brain Barrier Group, King’s College London, Strand, London, UK
2. Medicine, University College Dublin, Belfield, Dublin, Ireland
3. Neurometabolic Unit. Department of Neurology, Hospital Sant Joan de Déu, CIBERER and MetabERN, Barcelona, Spain
4. Chiesi Farmaceutici S.p.A, Parma, Italy
5. Regional Coordinating Center for Rare Diseases, Udine University Hospital, Udine, Italy
6. Laboratory of Diagnosis and Therapy of Lysosomal Disorders, Dept. of Women’s and Children’s Health, University of Padova, Padova, Italy
7. Istituto di Ricerca Pediatrica Città della Speranza, Padova, Italy
8. Nanotech Lab, Department of Life Sciences, University of Modena and Reggio Emilia, Modena, Italy