High-Density Recombinant Adeno-Associated Viral Particles are Competent Vectors forIn VivoTransduction-Reference-Cited by-同舟云学术

High-Density Recombinant Adeno-Associated Viral Particles are Competent Vectors forIn VivoTransduction

Published:2016-12 Issue:12 Volume:27 Page:971-981
ISSN:1043-0342
Container-title:Human Gene Therapy
language:en
Short-container-title:Human Gene Therapy

Author:

Wang Qizhao¹²,Firrman Jenni³⁴,Wu Zhongren²,Pokiniewski Katie A.³,Valencia C. Alexander⁵⁶,Wang Hairong⁷,Wei Hongying²,Zhuang Zhenjing¹²,Liu LinShu⁴,Wunder Stephanie L.⁷,Chin Mario P.S.¹,Xu Ruian¹,Diao Yong¹,Dong Biao²,Xiao Weidong¹²³⁴⁸

Affiliation:

1. Institute of Genomics, School of Biomedical Sciences, Huaqiao University, Quanzhou, China

2. Sol Sherry Thrombosis Research Center, Temple University, Philadelphia, Pennsylvania

3. Department of Microbiology and Immunology, Temple University, Philadelphia, Pennsylvania

4. United States Department of Agriculture, ARS, ERRC, Wyndmoor, Pennyslvania

5. Division of Human Genetics, Cincinnati Children's Hospital Medical Center, Cincinnati, Ohio

6. Department of Pediatrics, University of Cincinnati School of Medicine, Cincinnati, Ohio.

7. Department of Chemistry, Temple University, Philadelphia, Pennsylvania

8. Cardiovascular Research Center, Temple University, Philadelphia, Pennsylvania

Publisher

Mary Ann Liebert Inc

Subject

Genetics,Molecular Biology,Molecular Medicine

Link

http://www.liebertpub.com/doi/pdf/10.1089/hum.2016.055

Reference53 articles.

1. AAV2 Gene Therapy Readministration in Three Adults with Congenital Blindness

2. HumanRPE65Gene Therapy for Leber Congenital Amaurosis: Persistence of Early Visual Improvements and Safety at 1 Year

3. Retinal gene therapy in patients with choroideremia: initial findings from a phase 1/2 clinical trial

4. Phase 2 Clinical Trial of a Recombinant Adeno-Associated Viral Vector Expressing α1-Antitrypsin: Interim Results

5. Immune Responses to Intramuscular Administration of Alipogene Tiparvovec (AAV1-LPLS447X) in a Phase II Clinical Trial of Lipoprotein Lipase Deficiency Gene Therapy

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