Retinal gene therapy in patients with choroideremia: initial findings from a phase 1/2 clinical trial-Reference-Cited by-同舟云学术

Retinal gene therapy in patients with choroideremia: initial findings from a phase 1/2 clinical trial

Published:2014-03 Issue:9923 Volume:383 Page:1129-1137
ISSN:0140-6736
Container-title:The Lancet
language:en
Short-container-title:The Lancet

Author:

MacLaren Robert E,Groppe Markus,Barnard Alun R,Cottriall Charles L,Tolmachova Tanya,Seymour Len,Clark K Reed,During Matthew J,Cremers Frans P M,Black Graeme C M,Lotery Andrew J,Downes Susan M,Webster Andrew R,Seabra Miguel C

Publisher

Elsevier BV

Subject

General Medicine

Reference27 articles.

1. Ein Fall von Choroideremie;Mauthner;Ber Naturwissensch-med Ver Inssbruck,1872

2. Aberrant splicing of the CHM gene is a significant cause of choroideremia;Sankila;Nat Genet,1992

3. Cloning of a gene that is rearranged in patients with choroideraemia;Cremers;Nature,1990

4. Cloning and characterization of the human choroideremia gene;van Bokhoven;Hum Mol Genet,1994

5. Retinal degeneration in choroideremia: deficiency of rab geranylgeranyl transferase;Seabra;Science,1993

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