HumanRPE65Gene Therapy for Leber Congenital Amaurosis: Persistence of Early Visual Improvements and Safety at 1 Year-Reference-Cited by-同舟云学术

HumanRPE65Gene Therapy for Leber Congenital Amaurosis: Persistence of Early Visual Improvements and Safety at 1 Year

Published:2009-09 Issue:9 Volume:20 Page:999-1004
ISSN:1043-0342
Container-title:Human Gene Therapy
language:en
Short-container-title:Human Gene Therapy

Author:

Cideciyan Artur V.¹,Hauswirth William W.²³,Aleman Tomas S.¹,Kaushal Shalesh²,Schwartz Sharon B.¹,Boye Sanford L.²,Windsor Elizabeth A.M.¹,Conlon Thomas J.²,Sumaroka Alexander¹,Pang Ji-jing²,Roman Alejandro J.¹,Byrne Barry J.³,Jacobson Samuel G.¹

Affiliation:

1. Scheie Eye Institute, University of Pennsylvania, Philadelphia, PA 19104.

2. Department of Ophthalmology, University of Florida, Gainesville, FL 32610.

3. Powell Gene Therapy Center, University of Florida, Gainesville, FL 32610.

Publisher

Mary Ann Liebert Inc

Subject

Genetics,Molecular Biology,Molecular Medicine

Link

http://www.liebertpub.com/doi/pdf/10.1089/hum.2009.086

Reference20 articles.

1. Long-Term Restoration of Rod and Cone Vision by Single Dose rAAV-Mediated Gene Transfer to the Retina in a Canine Model of Childhood Blindness