1. Department of Pediatrics, Jikei University School of Medicine, Tokyo 105-8461, Japan.
2. Division of Gene Therapy, Research Center for Medical Sciences, Jikei University School of Medicine, Tokyo 105-8461, Japan.
3. Department of Pediatrics, Kitasato University School of Medicine, Kanagawa 252-0374, Japan.
4. Division of Neuropathology, Department of Pathology, Jikei University School of Medicine, Tokyo 105-8461, Japan.
5. Advanced Clinical Research Center, Institute of Neurological Disorders, Kanagawa 215-0026, Japan.