The status of hematopoietic stem cell transplantation in lysosomal storage disease

Author:

Malatack J.Jeffrey,Consolini Deborah M,Bayever Eliel

Publisher

Elsevier BV

Subject

Clinical Neurology,Developmental Neuroscience,Neurology,Pediatrics, Perinatology, and Child Health

Reference53 articles.

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5. Reversal of clinical features of Hurler's disease and biochemical improvement after treatment by bone-marrow transplantation;Hobbs;Lancet,1981

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