Non-invasive intravenous administration of AAV9 transducing iduronate sulfatase leads to global metabolic correction and prevention of neurologic deficits in a mouse model of Hunter syndrome-Reference-Cited by-同舟云学术

Non-invasive intravenous administration of AAV9 transducing iduronate sulfatase leads to global metabolic correction and prevention of neurologic deficits in a mouse model of Hunter syndrome

Published:2023-03 Issue: Volume:34 Page:100956
ISSN:2214-4269
Container-title:Molecular Genetics and Metabolism Reports
language:en
Short-container-title:Molecular Genetics and Metabolism Reports

Author:

Laoharawee Kanut,Podetz-Pedersen Kelly M.,Nguyen Tam T.,Singh Sajya M.,Smith Miles C.,Belur Lalitha R.,Low Walter C.,Kozarsky Karen F.,McIvor R. Scott

Publisher

Elsevier BV

Subject

Endocrinology,Genetics,Molecular Biology

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3. Therapeutic potential of lithium chloride and valproic acid against neuronopathic types of mucopolysaccharidoses through induction of the autophagy process;Archives of Biochemistry and Biophysics;2023-10