K137R Mutation on Adeno-Associated Viral Capsids Had Minimal Effect on Enhancing Gene DeliveryIn Vivo-Reference-Cited by-同舟云学术

K137R Mutation on Adeno-Associated Viral Capsids Had Minimal Effect on Enhancing Gene DeliveryIn Vivo

Published:2014-02 Issue:1 Volume:25 Page:33-39
ISSN:1946-6536
Container-title:Human Gene Therapy Methods
language:en
Short-container-title:Human Gene Therapy Methods

Author:

Qiao Chunping¹,Li Chengwen²,Zhao Chunxia¹³,Li Jianbin¹,Bian Tao¹,Grieger Joshua²,Li Juan¹,Samulski R. Jude²,Xiao Xiao¹

Affiliation:

1. Division of Molecular Pharmaceutics, Eshelman School of Pharmacy, University of North Carolina at Chapel Hill, Chapel Hill, NC 27599.

2. Gene Therapy Center, Department of Pediatrics, University of North Carolina at Chapel Hill, Chapel Hill, NC 27599.

3. Cardiovascular Division of Internal Medicine, Tongji Hospital, Tongji Medical College, Huazhong University of Science and Technology, Wuhan 430030, P.R. China.

Publisher

Mary Ann Liebert Inc

Subject

Genetics (clinical),Pharmacology,Genetics,Applied Microbiology and Biotechnology,Molecular Medicine

Link

http://www.liebertpub.com/doi/pdf/10.1089/hgtb.2013.176

Reference42 articles.

1. Reengineering a receptor footprint of adeno-associated virus enables selective and systemic gene transfer to muscle

2. High AAV vector purity results in serotype- and tissue-independent enhancement of transduction efficiency

3. Adeno-Associated Virus (AAV) Serotype 9 Provides Global Cardiac Gene Transfer Superior to AAV1, AAV6, AAV7, and AAV8 in the Mouse and Rat

4. Phase 1 Gene Therapy for Duchenne Muscular Dystrophy Using a Translational Optimized AAV Vector

5. Enhanced gene delivery to the neonatal retina through systemic administration of tyrosine-mutated AAV9

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2. AAV Vector-Based Gene Therapy, Progress and Current Challenges;Safety and Efficacy of Gene-Based Therapeutics for Inherited Disorders;2017

3. Single point mutation in adeno-associated viral vectors -DJ capsid leads to improvement for gene delivery in vivo;BMC Biotechnology;2016-01-05

4. Site-Directed Mutagenesis of Surface-Exposed Lysine Residues Leads to Improved Transduction by AAV2, But Not AAV8, Vectors in Murine Hepatocytes In Vivo;Human Gene Therapy Methods;2015-12

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