Basic and Clinical Application of Adeno-Associated Virus–Mediated Genome Editing-Reference-Cited by-同舟云学术

Basic and Clinical Application of Adeno-Associated Virus–Mediated Genome Editing

Published:2019-06 Issue:6 Volume:30 Page:673-681
ISSN:1043-0342
Container-title:Human Gene Therapy
language:en
Short-container-title:Human Gene Therapy

Author:

He Xiubin¹,Xie Haihua¹,Liu Xiexie¹,Gu Feng¹

Affiliation:

1. School of Ophthalmology and Optometry, Eye Hospital, Wenzhou Medical University, State Key Laboratory and Key Laboratory of Vision Science, Ministry of Health and Zhejiang Provincial Key Laboratory of Ophthalmology and Optometry, Wenzhou, P.R. China.

Publisher

Mary Ann Liebert Inc

Subject

Genetics,Molecular Biology,Molecular Medicine

Link

https://www.liebertpub.com/doi/pdf/10.1089/hum.2018.190

Reference105 articles.

1. Monogenic and polygenic determinants of sarcoma risk: an international genetic study

2. Immune Responses to Intramuscular Administration of Alipogene Tiparvovec (AAV1-LPLS447X) in a Phase II Clinical Trial of Lipoprotein Lipase Deficiency Gene Therapy

3. Long-Term Safety and Efficacy of Factor IX Gene Therapy in Hemophilia B

4. Retinal gene therapy in patients with choroideremia: initial findings from a phase 1/2 clinical trial

5. Cardiac AAV9-S100A1 Gene Therapy Rescues Post-Ischemic Heart Failure in a Preclinical Large Animal Model

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