Targeting Translation Termination Machinery with Antisense Oligonucleotides for Diseases Caused by Nonsense Mutations
Author:
Affiliation:
1. Ionis Pharmaceuticals, Carlsbad, California.
Publisher
Mary Ann Liebert Inc
Subject
Drug Discovery,Genetics,Molecular Biology,Molecular Medicine,Biochemistry
Link
https://www.liebertpub.com/doi/pdf/10.1089/nat.2019.0779
Reference57 articles.
1. A meta-analysis of nonsense mutations causing human genetic disease
2. Nonsense-mediated RNA decay in the brain: emerging modulator of neural development and disease
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