Systemic Correction of a Fatty Acid Oxidation Defect by Intramuscular Injection of a Recombinant Adeno-Associated Virus Vector-Reference-Cited by-同舟云学术

Systemic Correction of a Fatty Acid Oxidation Defect by Intramuscular Injection of a Recombinant Adeno-Associated Virus Vector

Published:2006-01 Issue:1 Volume:17 Page:71-80
ISSN:1043-0342
Container-title:Human Gene Therapy
language:en
Short-container-title:Human Gene Therapy

Author:

Conlon Thomas J.¹,Walter Glenn²,Owen Renius¹,Cossette Travis¹,Erger Kirsten¹,Gutierrez Greg²,Goetzman Eric³,Matern Dietrich⁴,Vockley Jerry³,Flotte Terence R.¹

Affiliation:

1. Department of Pediatrics, Powell Gene Therapy Center, University of Florida, Gainesville, FL 32610.

2. Department of Physiology and Functional Genomics, McKnight Brain Institute, and Powell Gene Therapy Center, University of Florida, Gainesville, FL 32610.

3. Department of Pediatrics, School of Medicine, University of Pittsburgh, Children's Hospital of Pittsburgh, Pittsburgh, PA.

4. Biochemical Genetics Laboratory, Division of Laboratory Genetics, Department of Laboratory Medicine and Pathology, Mayo Clinic College of Medicine, Rochester, MN.

Publisher

Mary Ann Liebert Inc

Subject

Genetics,Molecular Biology,Molecular Medicine

Link

http://www.liebertpub.com/doi/pdf/10.1089/hum.2006.17.71

Reference29 articles.

1. Short-Chain Acyl-Coenzyme A Dehydrogenase Activity, Antigen, and Biosynthesis Are Absent in the BALB/cByJ Mouse

2. Cytotoxic Immune Response After Retroviral-Mediated Hepatic Gene Transfer in Rat Does Not Preclude Expression from Adeno-Associated Virus 1 Transduced Muscles

3. Transduced CD34+ cells from adrenoleukodystrophy patients with HIV-derived vector mediate long-term engraftment of NOD/SCID mice

4. Retroviral-mediated gene transfer corrects very-long-chain fatty acid metabolism in adrenoleukodystrophy fibroblasts.

Cited by 15 articles. 订阅此论文施引文献订阅此论文施引文献，注册后可以免费订阅5篇论文的施引文献，订阅后可以查看论文全部施引文献

1. 2-Bromopalmitate depletes lipid droplets to inhibit viral replication;Journal of Virology;2024-04-16

2. Uncovering the Vital Role of Lipid Droplets in Coronavirus Replication: A Novel Insight Arising from the Biological Activity of 2-Bromopalmitate;2023-06-30

3. Adeno-Associated Virus–Mediated Gene Therapy for Metabolic Myopathy;Human Gene Therapy;2013-11

4. Cell and Gene Therapy for Genetic Diseases: Inherited Disorders Affecting the Lung and Those Mimicking Sudden Infant Death Syndrome;Human Gene Therapy;2012-06

5. Long-term Correction of Very Long-chain Acyl-CoA Dehydrogenase Deficiency in Mice Using AAV9 Gene Therapy;Molecular Therapy;2012-06