Transduced CD34+ cells from adrenoleukodystrophy patients with HIV-derived vector mediate long-term engraftment of NOD/SCID mice-Reference-Cited by-同舟云学术

Transduced CD34+ cells from adrenoleukodystrophy patients with HIV-derived vector mediate long-term engraftment of NOD/SCID mice

Published:2003-03 Issue:3 Volume:7 Page:317-324
ISSN:1525-0016
Container-title:Molecular Therapy
language:en
Short-container-title:Molecular Therapy

Author:

Benhamida Sonia,Pflumio Françoise,Dubart-Kupperschmitt Anne,Zhao-Emonet Jing-Chao,Cavazzana-Calvo Marina,Rocchiccioli Francis,Fichelson Serge,Aubourg Patrick,Charneau Pierre,Cartier Nathalie

Publisher

Elsevier BV

Subject

Drug Discovery,Pharmacology,Genetics,Molecular Biology,Molecular Medicine

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3. Expression of the adrenoleukodystrophy protein in the human and mouse central nervous system;Fouquet;Neurobiol. Dis.,1997

4. Putative X-linked adrenoleukodystrophy gene shares unexpected homology with ABC transporters;Mosser;Nature,1993

5. Reversal of early neurologic and neuroradiologic manifestations of X-linked adrenoleukodystrophy by bone marrow transplantation;Aubourg;N. Engl. J. Med.,1990

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