Long-term Correction of Very Long-chain Acyl-CoA Dehydrogenase Deficiency in Mice Using AAV9 Gene Therapy-Reference-Cited by-同舟云学术

Long-term Correction of Very Long-chain Acyl-CoA Dehydrogenase Deficiency in Mice Using AAV9 Gene Therapy

Published:2012-06 Issue:6 Volume:20 Page:1131-1138
ISSN:1525-0016
Container-title:Molecular Therapy
language:en
Short-container-title:Molecular Therapy

Author:

Keeler Allison M,Conlon Thomas,Walter Glenn,Zeng Huadong,Shaffer Scott A,Dungtao Fu,Erger Kirsten,Cossette Travis,Tang Qiushi,Mueller Christian,Flotte Terence R

Publisher

Elsevier BV

Subject

Drug Discovery,Pharmacology,Genetics,Molecular Biology,Molecular Medicine

Reference34 articles.

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3. Mitochondrial very-long-chain acyl-coenzyme A dehydrogenase deficiency: clinical characteristics and diagnostic considerations in 30 patients;Vianey-Saban;Clin Chim Acta,1998

4. Very long chain acyl-coenzyme A dehydrogenase deficiency with adult onset;Smelt;Ann Neurol,1998

5. Mutation analysis in mitochondrial fatty acid oxidation defects: Exemplified by acyl-CoA dehydrogenase deficiencies, with special focus on genotype-phenotype relationship;Gregersen;Hum Mutat,2001

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