Magnetic Resonance Imaging-Guided Delivery of Adeno-Associated Virus Type 2 to the Primate Brain for the Treatment of Lysosomal Storage Disorders-Reference-Cited by-同舟云学术

Magnetic Resonance Imaging-Guided Delivery of Adeno-Associated Virus Type 2 to the Primate Brain for the Treatment of Lysosomal Storage Disorders

Published:2010-09 Issue:9 Volume:21 Page:1093-1103
ISSN:1043-0342
Container-title:Human Gene Therapy
language:en
Short-container-title:Human Gene Therapy

Author:

Salegio E. Aguilar¹,Kells A.P.¹,Richardson R.M.¹,Hadaczek P.¹,Forsayeth J.¹,Bringas J.¹,Sardi S.P.²,Passini M.A.²,Shihabuddin L.S.²,Cheng S.H.²,Fiandaca M.S.¹,Bankiewicz K.S.¹

Affiliation:

1. Department of Neurosurgery, University of California San Francisco, San Francisco, CA 94103.

2. Genzyme, Framingham, MA 01701.

Publisher

Mary Ann Liebert Inc

Subject

Genetics,Molecular Biology,Molecular Medicine

Link

http://www.liebertpub.com/doi/pdf/10.1089/hum.2010.040

Reference43 articles.

1. Long-Term Clinical Improvement in MPTP-Lesioned Primates after Gene Therapy with AAV-hAADC

2. AAV8-Mediated Hepatic Expression of Acid Sphingomyelinase Corrects the Metabolic Defect in the Visceral Organs of a Mouse Model of Niemann–Pick Disease

3. Gene therapy for lysosomal storage disorders

4. Selective and Rapid Uptake of Adeno-Associated Virus Type 2 in Brain

5. Replacement Therapy for Inherited Enzyme Deficiency — Macrophage-Targeted Glucocerebrosidase for Gaucher's Disease

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