Adeno-Associated Virus Delivery Limitations for Neurological Indications
Author:
Affiliation:
1. Horae Gene Therapy Center, University of Massachusetts Chan Medical School, Worcester, Massachusetts, USA.
2. Department of Radiology, University of Massachusetts Chan Medical School, Worcester, Massachusetts, USA.
Publisher
Mary Ann Liebert Inc
Subject
Genetics,Molecular Biology,Molecular Medicine
Link
https://www.liebertpub.com/doi/pdf/10.1089/hum.2022.29196.hrb
Reference106 articles.
1. History of gene therapy
2. Dual-AAV delivery of large gene sequences to the inner ear
3. Adeno-associated virus vector carrying human minidystrophin genes effectively ameliorates muscular dystrophy in mdx mouse model
4. Feasibility of using NF1-GRD and AAV for gene replacement therapy in NF1-associated tumors
5. MicroRNA as a Therapeutic Target in Cardiac Remodeling
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