Feasibility of Targeted Delivery of AAV5-GFP into the Cerebellum of Nonhuman Primates Following a Single Convection-Enhanced Delivery Infusion-Reference-Cited by-同舟云学术

Feasibility of Targeted Delivery of AAV5-GFP into the Cerebellum of Nonhuman Primates Following a Single Convection-Enhanced Delivery Infusion

Published:2022-01-01 Issue:1-2 Volume:33 Page:86-93
ISSN:1043-0342
Container-title:Human Gene Therapy
language:en
Short-container-title:Human Gene Therapy

Author:

Salegio Ernesto A.¹^ORCID,Cukrov Mira¹,Lortz Rachel¹,Green Abigail¹,Lambert Emily¹,Copeland Summer¹,Gonzalez Marc¹,Stockinger Diane E.¹,Yeung Jeremy M.¹,Hwa Granger G.C.¹

Affiliation:

1. Valley Biosystems, Inc., West Sacramento, California, USA.

Publisher

Mary Ann Liebert Inc

Subject

Genetics,Molecular Biology,Molecular Medicine

Link

https://www.liebertpub.com/doi/pdf/10.1089/hum.2021.163

Reference41 articles.

1. Adeno-associated virus vector as a platform for gene therapy delivery

2. The AAV Vector Toolkit: Poised at the Clinical Crossroads

3. Comparison of the ability of adeno-associated viral vectors pseudotyped with serotype 2, 5, and 8 capsid proteins to mediate efficient transduction of the liver in murine and nonhuman primate models

4. Axonal transport of adeno-associated viral vectors is serotype-dependent

5. Recombinant AAV Viral Vectors Pseudotyped with Viral Capsids from Serotypes 1, 2, and 5 Display Differential Efficiency and Cell Tropism after Delivery to Different Regions of the Central Nervous System

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3. Pre-clinical delivery of gene therapy products to the cerebrospinal fluid: challenges and considerations for clinical translation;Frontiers in Molecular Neuroscience;2023-08-17

4. Incisionless targeted adeno-associated viral vector delivery to the brain by focused ultrasound-mediated intranasal administration;eBioMedicine;2022-10