1. University of California San Diego, San Diego, California, United States
2. The Center for Inherited Blood Disorders, Orange, California, United States
3. University of California, Davis, Sacramento, California, United States
4. Center for Bleeding Disorders and Coagulation, Florence, Italy
5. University of North Carolina at Chapel Hill, Chapel Hill, North Carolina, United States
6. Oregon Health & Science University, Portland, Oregon, United States
7. Erasmus MC, University Medical Center Rotterdam, Rotterdam, Netherlands
8. University Hospital Frankfurt, Germany
9. American Thrombosis and Hemostasis Network, United States
10. uniQure Inc, Naples, Florida, United States
11. uniQure, Lexington, Massachusetts, United States
12. CSL Behring, King of Prussia, Pennsylvania, United States
13. CSL Behring (Europe), Hattersheim am Main, California, Germany
14. Yale University School of Medicine, United States