Tuning protein folding in lysosomal storage diseases: the chemistry behind pharmacological chaperones
Author:
Affiliation:
1. REQUIMTE/LAQV
2. Laboratório de Farmacognosia
3. Departamento de Química
4. Faculdade de Farmácia
5. Universidade do Porto
Abstract
We review pharmacological chaperones used in lysosomal storage diseases, emphasizing medicinal chemistry approaches and mechanisms of action.
Publisher
Royal Society of Chemistry (RSC)
Subject
General Chemistry
Link
http://pubs.rsc.org/en/content/articlepdf/2018/SC/C7SC04712F
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