Meganuclease targeting of PCSK9 in macaque liver leads to stable reduction in serum cholesterol-Reference-Cited by-同舟云学术

Meganuclease targeting of PCSK9 in macaque liver leads to stable reduction in serum cholesterol

Published:2018-07-09 Issue:8 Volume:36 Page:717-725
ISSN:1087-0156
Container-title:Nature Biotechnology
language:en
Short-container-title:Nat Biotechnol

Author:

Wang Lili,Smith Jeff,Breton Camilo,Clark Peter,Zhang Jia,Ying Lei,Che Yan,Lape Janel,Bell Peter,Calcedo Roberto,Buza Elizabeth L,Saveliev Alexei,Bartsevich Victor V,He Zhenning,White John,Li Mingyao,Jantz Derek,Wilson James M

Publisher

Springer Science and Business Media LLC

Subject

Biomedical Engineering,Molecular Medicine,Applied Microbiology and Biotechnology,Bioengineering,Biotechnology

Link

http://www.nature.com/articles/nbt.4182.pdf

Reference61 articles.

1. Li, H. et al. In vivo genome editing restores haemostasis in a mouse model of haemophilia. Nature 475, 217–221 (2011).

2. Barzel, A. et al. Promoterless gene targeting without nucleases ameliorates haemophilia B in mice. Nature 517, 360–364 (2015).

3. Ran, F.A. et al. In vivo genome editing using Staphylococcus aureus Cas9. Nature 520, 186–191 (2015).

4. Nelson, C.E. et al. In vivo genome editing improves muscle function in a mouse model of Duchenne muscular dystrophy. Science 351, 403–407 (2016).

5. Long, C. et al. Postnatal genome editing partially restores dystrophin expression in a mouse model of muscular dystrophy. Science 351, 400–403 (2016).

Cited by 100 articles. 订阅此论文施引文献订阅此论文施引文献，注册后可以免费订阅5篇论文的施引文献，订阅后可以查看论文全部施引文献

1. Modulation of AAV9 Galactose Binding Yields Novel Gene Therapy Vectors and Predicts Cross-Species Differences in Glycan Avidity;Human Gene Therapy;2024-08-13

2. Gene editing in liver diseases;FEBS Letters;2024-07-30

3. Fast and facile synthesis of amidine-incorporated degradable lipids for versatile mRNA delivery in vivo;Nature Chemistry;2024-07-09

4. The importance of LDL-C lowering in atherosclerotic cardiovascular disease prevention: Lower for longer is better;American Journal of Preventive Cardiology;2024-06

5. A temperature-sensitive and interferon-silent Sendai virus vector for CRISPR-Cas9 delivery and gene editing in primary human cells;2024-05-05