In vivo genome editing restores haemostasis in a mouse model of haemophilia-Reference-Cited by-同舟云学术

In vivo genome editing restores haemostasis in a mouse model of haemophilia

Published:2011-06-26 Issue:7355 Volume:475 Page:217-221
ISSN:0028-0836
Container-title:Nature
language:en
Short-container-title:Nature

Author:

Li Hojun,Haurigot Virginia,Doyon Yannick,Li Tianjian,Wong Sunnie Y.,Bhagwat Anand S.,Malani Nirav,Anguela Xavier M.,Sharma Rajiv,Ivanciu Lacramiora,Murphy Samuel L.,Finn Jonathan D.,Khazi Fayaz R.,Zhou Shangzhen,Paschon David E.,Rebar Edward J.,Bushman Frederic D.,Gregory Philip D.,Holmes Michael C.,High Katherine A.

Publisher

Springer Science and Business Media LLC

Subject

Multidisciplinary

Link

http://www.nature.com/articles/nature10177.pdf

Reference30 articles.

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2. Urnov, F. D. et al. Highly efficient endogenous human gene correction using designed zinc-finger nucleases. Nature 435, 646–651 (2005)

3. Porteus, M. H. & Baltimore, D. Chimeric nucleases stimulate gene targeting in human cells. Science 300, 763 (2003)

4. Bibikova, M. et al. Stimulation of homologous recombination through targeted cleavage by chimeric nucleases. Mol. Cell. Biol. 21, 289–297 (2001)

5. Cartier, N. et al. Hematopoietic stem cell gene therapy with a lentiviral vector in X-linked adrenoleukodystrophy. Science 326, 818–823 (2009)

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