A high-fidelity Cas9 mutant delivered as a ribonucleoprotein complex enables efficient gene editing in human hematopoietic stem and progenitor cells-Reference-Cited by-同舟云学术

A high-fidelity Cas9 mutant delivered as a ribonucleoprotein complex enables efficient gene editing in human hematopoietic stem and progenitor cells

Published:2018-08 Issue:8 Volume:24 Page:1216-1224
ISSN:1078-8956
Container-title:Nature Medicine
language:en
Short-container-title:Nat Med

Author:

Vakulskas Christopher A.^ORCID,Dever Daniel P.,Rettig Garrett R.^ORCID,Turk Rolf^ORCID,Jacobi Ashley M.^ORCID,Collingwood Michael A.^ORCID,Bode Nicole M.^ORCID,McNeill Matthew S.,Yan Shuqi,Camarena Joab,Lee Ciaran M.^ORCID,Park So Hyun,Wiebking Volker^ORCID,Bak Rasmus O.^ORCID,Gomez-Ospina Natalia^ORCID,Pavel-Dinu Mara,Sun Wenchao^ORCID,Bao Gang,Porteus Matthew H.,Behlke Mark A.^ORCID

Publisher

Springer Science and Business Media LLC

Subject

General Biochemistry, Genetics and Molecular Biology,General Medicine

Link

http://www.nature.com/articles/s41591-018-0137-0.pdf

Reference73 articles.

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3. Doudna, J. A. & Charpentier, E. Genome editing. The new frontier of genome engineering with CRISPR–Cas9. Science 346, 1258096 (2014).

4. Hsu, P. D., Lander, E. S. & Zhang, F. Development and applications of CRISPR–Cas9 for genome engineering. Cell 157, 1262–1278 (2014).

5. Dagdas, Y. S. et al. A conformational checkpoint between DNA binding and cleavage by CRISPR–Cas9. Sci. Adv. 3, eaao0027 (2017).

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