Therapeutic Response in Feline Sandhoff Disease Despite Immunity to Intracranial Gene Therapy-Reference-Cited by-同舟云学术

Therapeutic Response in Feline Sandhoff Disease Despite Immunity to Intracranial Gene Therapy

Published:2013-07 Issue:7 Volume:21 Page:1306-1315
ISSN:1525-0016
Container-title:Molecular Therapy
language:en
Short-container-title:Molecular Therapy

Author:

Bradbury Allison M,Cochran J Nicholas,McCurdy Victoria J,Johnson Aime K,Brunson Brandon L,Gray-Edwards Heather,Leroy Stanley G,Hwang Misako,Randle Ashley N,Jackson Laura S,Morrison Nancy E,Baek Rena C,Seyfried Thomas N,Cheng Seng H,Cox Nancy R,Baker Henry J,Cachón-González M Begona,Cox Timothy M,Sena-Esteves Miguel,Martin Douglas R

Publisher

Elsevier BV

Subject

Drug Discovery,Pharmacology,Genetics,Molecular Biology,Molecular Medicine

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5. Inefficiency in GM2 ganglioside elimination by human lysosomal beta-hexosaminidase beta-subunit gene transfer to fibroblastic cell line derived from Sandhoff disease model mice;Itakura;Biol Pharm Bull,2006

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