Bicistronic lentiviral vector corrects β-hexosaminidase deficiency in transduced and cross-corrected human Sandhoff fibroblasts-Reference-Cited by-同舟云学术

Bicistronic lentiviral vector corrects β-hexosaminidase deficiency in transduced and cross-corrected human Sandhoff fibroblasts

Published:2005-11 Issue:2 Volume:20 Page:583-593
ISSN:0969-9961
Container-title:Neurobiology of Disease
language:en
Short-container-title:Neurobiology of Disease

Author:

Arfi Audrey,Bourgoin Christophe,Basso Luisa,Emiliani Carla,Tancini Brunella,Chigorno Vanna,Li Yu-Teh,Orlacchio Aldo,Poenaru Livia,Sonnino Sandro,Caillaud Catherine

Publisher

Elsevier BV

Subject

Neurology

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5. Synthesis of 4-methylumbelliferyl-beta-d-N-acetylglucosamine-6-sulfate and its use in classification of GM2 gangliosidosis genotypes;Bayleran;Clin. Chim. Acta,1984

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