Correction of ADAMTS13 Deficiency by In Utero Gene Transfer of Lentiviral Vector encoding ADAMTS13 Genes-Reference-Cited by-同舟云学术

Correction of ADAMTS13 Deficiency by In Utero Gene Transfer of Lentiviral Vector encoding ADAMTS13 Genes

Published:2009-01 Issue:1 Volume:17 Page:34-41
ISSN:1525-0016
Container-title:Molecular Therapy
language:en
Short-container-title:Molecular Therapy

Author:

Niiya Masami,Endo Masayuki,Shang Dezhi,Zoltick Philip W,Muvarak Nidal E,Cao Wenjing,Jin Sheng-Yu,Skipwith Christopher G,Motto David G,Flake Alan W,Zheng X Long

Publisher

Elsevier BV

Subject

Drug Discovery,Pharmacology,Genetics,Molecular Biology,Molecular Medicine

Reference47 articles.

1. Mutations in a member of the ADAMTS gene family cause thrombotic thrombocytopenic purpura;Levy;Nature,2001

2. Structure of von Willebrand factor-cleaving protease (ADAMTS13), a metalloprotease involved in thrombotic thrombocytopenic purpura;Zheng;J Biol Chem,2001

3. Physiologic cleavage of von Willebrand factor by a plasma protease is dependent on its conformation and requires calcium ion;Tsai;Blood,1996

4. Cleavage of von Willebrand factor requires the spacer domain of the metalloprotease ADAMTS13;Zheng;J Biol Chem,2003

5. The proximal carboxyl-terminal domains of ADAMTS13 determine substrate specificity and are all required for cleavage of von Willebrand factor;Ai;J Biol Chem,2005

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