A Review of Gene, Drug and Cell-Based Therapies for Usher Syndrome
Author:
Publisher
Frontiers Media SA
Subject
Cellular and Molecular Neuroscience
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1. Generation of two induced pluripotent stem cell lines from an Usher syndrome type 1B patient with the homozygous c.496del MYO7A variant;Stem Cell Research;2024-09
2. Adaptive optics retinal imaging in patients with usher syndrome;Frontiers in Ophthalmology;2024-05-28
3. Usher syndrome: Genetic diagnosis and current therapeutic approaches;World Journal of Otorhinolaryngology;2024-01-19
4. Recent Therapeutic Progress and Future Perspectives for the Treatment of Hearing Loss;Biomedicines;2023-12-18
5. PCDH15 Dual-AAV Gene Therapy for Deafness and Blindness in Usher Syndrome Type 1F;2023-11-13
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