Therapy for lysosomal storage disorders
Author:
Publisher
Wiley
Subject
Cell Biology,Clinical Biochemistry,Genetics,Molecular Biology,Biochemistry
Link
http://onlinelibrary.wiley.com/wol1/doi/10.1002/iub.284/fullpdf
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3. Allogeneic stem cell transplantation for the treatment of lysosomal and peroxisomal metabolic diseases;Krivit;Springer Semin. Immunopathol.,2004
4. Hematopoietic cell transplantation for inherited metabolic diseases: an overview of outcomes and practice guidelines;Peters;Bone Marrow Transplant.,2003
5. Cord-blood transplants from unrelated donors in patients with Hurler's syndrome;Staba;N. Engl. J. Med.,2004
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