A novel strategy for delivering <scp>N</scp> iemann‐ <scp>P</scp> ick type <scp>C2</scp> proteins across the blood–brain barrier using the brain endothelial‐specific <scp>AAV‐BR1</scp> virus-Reference-Cited by-同舟云学术

A novel strategy for delivering N iemann‐ P ick type C2 proteins across the blood–brain barrier using the brain endothelial‐specific AAV‐BR1 virus

Published:2022-05-25 Issue:1 Volume:164 Page:6-28
ISSN:0022-3042
Container-title:Journal of Neurochemistry
language:en
Short-container-title:Journal of Neurochemistry

Author:

Rasmussen Charlotte Laurfelt Munch¹^ORCID,Hede Eva¹^ORCID,Routhe Lisa Juul¹^ORCID,Körbelin Jakob²^ORCID,Helgudottir Steinunn Sara¹^ORCID,Thomsen Louiza Bohn¹^ORCID,Schwaninger Markus³^ORCID,Burkhart Annette¹^ORCID,Moos Torben¹^ORCID

Affiliation:

1. Neurobiology Research and Drug Delivery, Department of Health Science and Technology Aalborg University Aalborg Denmark

2. Department of Oncology, Hematology and Bone Marrow Transplantation University Medical Center Hamburg Germany

3. Institute for Experimental and Clinical Pharmacology and Toxicology University of Lübeck Lübeck Germany

Funder

Hørslev-Fonden

Oda og Hans Svenningsens Fond

Torben og Alice Frimodts Fond

Civilingeniør Frode V. Nyegaard og Hustrus Fond

Svend Andersen Fonden

Lundbeckfonden

Aalborg Universitet

Publisher

Wiley

Subject

Cellular and Molecular Neuroscience,Biochemistry

Link

https://onlinelibrary.wiley.com/doi/pdf/10.1111/jnc.15621

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