Characterization of a HIR-Fab-IDS, Novel Iduronate 2-Sulfatase Fusion Protein for the Treatment of Neuropathic Mucopolysaccharidosis Type II (Hunter Syndrome)-Reference-Cited by-同舟云学术

Characterization of a HIR-Fab-IDS, Novel Iduronate 2-Sulfatase Fusion Protein for the Treatment of Neuropathic Mucopolysaccharidosis Type II (Hunter Syndrome)

Published:2023-04-04 Issue:3 Volume:37 Page:375-395
ISSN:1173-8804
Container-title:BioDrugs
language:en
Short-container-title:BioDrugs

Author:

Gusarova Valentina D.^ORCID,Smolov Maxim A.^ORCID,Lyagoskin Ivan V.^ORCID,Degterev Maksim B.^ORCID,Rechetnik Elizaveta V.,Rodionov Alexander V.,Pantyushenko Marina S.,Shukurov Rahim R.^ORCID

Publisher

Springer Science and Business Media LLC

Subject

Pharmacology (medical),Pharmacology,General Medicine,Biotechnology

Link

https://link.springer.com/content/pdf/10.1007/s40259-023-00590-w.pdf

Reference54 articles.

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3. Desnick RJ, Schuchman EH. Enzyme replacement therapy for lysosomal diseases: lessons from 20 years of experience and remaining challenges. Annu Rev Genomics Hum Genet. 2012;13:307–35. https://doi.org/10.1146/annurev-genom-090711-163739.

4. Scarpa M, Bellettato CM, Lampe C, Begley DJ. Neuronopathic lysosomal storage disorders: approaches to treat the central nervous system. Best Pract Res Clin Endocrinol Metab. 2015;29:159–71. https://doi.org/10.1016/j.beem.2014.12.001.

5. Tokic V, Barisic I, Huzjak N, et al. Enzyme replacement therapy in two patients with an advanced severe (Hurler) phenotype of mucopolysaccharidosis I. Eur J Pediatr. 2007;166:727–32. https://doi.org/10.1007/s00431-006-0316-8.

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