Sapropterin dihydrochloride for phenylketonuria
Author:
Publisher
John Wiley & Sons, Ltd
Link
https://www.cochranelibrary.com/cdsr/doi/10.1002/14651858.CD008005.pub2/epdf/full
Reference44 articles.
1. Lee P Treacy EP Crombez E Wasserstein M Waber L Wolff J Safety and efficacy of 22 weeks of treatment with sapropterin dihydrochloride in patients with phenylketonuria American Journal of Medical Genetics. Part A 2008 2851 9
2. A phase 3 study of the efficacy of sapropterin in reducing phe levels in subjects with phenylketonuria [abstract];Levy;Journal of Inherited Metabolic Disease,2006
3. Efficacy of sapropterin dihydrochloride (tetrahydrobiopterin, 6R-BH4) for reduction of phenylalanine concentration in patients with phenylketonuria: a phase III randomised placebo-controlled study;Levy;Lancet,2007
4. Efficacy of sapropterin dihydrochloride in increasing phenylalanine tolerance in children with phenylketonuria: a phase III, randomized, double-blind, placebo-controlled study;Trefz;Journal of Pediatrics,2009
5. Management of phenylketonuria and hyperphenylalaninemia;Baulny;Journal of Nutrition,2007
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