Efficacy of Sapropterin Dihydrochloride in Increasing Phenylalanine Tolerance in Children with Phenylketonuria: A Phase III, Randomized, Double-Blind, Placebo-Controlled Study-Reference-Cited by-同舟云学术

Efficacy of Sapropterin Dihydrochloride in Increasing Phenylalanine Tolerance in Children with Phenylketonuria: A Phase III, Randomized, Double-Blind, Placebo-Controlled Study

Published:2009-05 Issue:5 Volume:154 Page:700-707.e1
ISSN:0022-3476
Container-title:The Journal of Pediatrics
language:en
Short-container-title:The Journal of Pediatrics

Author:

Trefz Friedrich K.,Burton Barbara K.,Longo Nicola,Casanova Mercedes Martinez-Pardo,Gruskin Daniel J.,Dorenbaum Alex,Kakkis Emil D.,Crombez Eric A.,Grange Dorothy K.,Harmatz Paul,Lipson Mark H.,Milanowski Andrzej,Randolph Linda Marie,Vockley Jerry,Whitley Chester B.,Wolff Jon A.,Bebchuk Judith,Christ-Schmidt Heidi,Hennermann Julia B.

Publisher

Elsevier BV

Subject

Pediatrics, Perinatology, and Child Health

Reference35 articles.

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3. Timing is everything: executive functions in children exposed to elevated levels of phenylalanine;Antshel;Neuropsychology,2003

4. Prefrontal cortex cognitive deficits in children treated early and continuously for PKU;Diamond;Monogr Soc Res Child Dev,1997

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